COMPOUND HAVING READTHROUGH ACTIVITY AND PHARMACEUTICAL COMPOSITION CONTAINING THE COMPOUND リードスルー活性を有する化合物及び該化合物を含む医薬組成物 - 特許庁
To provide a novel compound having readthrough activity and a therapeutic agent for diseases caused by nonsense mutations which contains the derivative. リードスルー活性を有する新規化合物及び該誘導体を含むナンセンス突然変異型疾患の治療薬の提供。 - 特許庁